Any news regarding PTC124?

miesl

New member
I haven't seen anything recently - but have you joined the mailing list on the PTC website? It looks like they mail out updates when they have them.

I don't know much about clinical studies with infants since they are limited on quality of life feedback and spirometry - but I would mention to your CF doc that you're interested in participating in studies if your daughter qualifies. I would assume that based on the favorable Phase 2 studies, PTC will be moving to Phase 3 soon and need more people for testing.

Studies are wonderful to participate in! Not only can you get experimental meds and treatment options - some of them pay quite nicely.

-Michelle
 

miesl

New member
I haven't seen anything recently - but have you joined the mailing list on the PTC website? It looks like they mail out updates when they have them.

I don't know much about clinical studies with infants since they are limited on quality of life feedback and spirometry - but I would mention to your CF doc that you're interested in participating in studies if your daughter qualifies. I would assume that based on the favorable Phase 2 studies, PTC will be moving to Phase 3 soon and need more people for testing.

Studies are wonderful to participate in! Not only can you get experimental meds and treatment options - some of them pay quite nicely.

-Michelle
 

miesl

New member
I haven't seen anything recently - but have you joined the mailing list on the PTC website? It looks like they mail out updates when they have them.

I don't know much about clinical studies with infants since they are limited on quality of life feedback and spirometry - but I would mention to your CF doc that you're interested in participating in studies if your daughter qualifies. I would assume that based on the favorable Phase 2 studies, PTC will be moving to Phase 3 soon and need more people for testing.

Studies are wonderful to participate in! Not only can you get experimental meds and treatment options - some of them pay quite nicely.

-Michelle
 

miesl

New member
I haven't seen anything recently - but have you joined the mailing list on the PTC website? It looks like they mail out updates when they have them.

I don't know much about clinical studies with infants since they are limited on quality of life feedback and spirometry - but I would mention to your CF doc that you're interested in participating in studies if your daughter qualifies. I would assume that based on the favorable Phase 2 studies, PTC will be moving to Phase 3 soon and need more people for testing.

Studies are wonderful to participate in! Not only can you get experimental meds and treatment options - some of them pay quite nicely.

-Michelle
 

miesl

New member
I haven't seen anything recently - but have you joined the mailing list on the PTC website? It looks like they mail out updates when they have them.
<br />
<br />I don't know much about clinical studies with infants since they are limited on quality of life feedback and spirometry - but I would mention to your CF doc that you're interested in participating in studies if your daughter qualifies. I would assume that based on the favorable Phase 2 studies, PTC will be moving to Phase 3 soon and need more people for testing.
<br />
<br />Studies are wonderful to participate in! Not only can you get experimental meds and treatment options - some of them pay quite nicely.
<br />
<br />-Michelle
 

NoExcuses

New member
Marla you have probably seen this before but the CFF updates this pipeline regularly <img src="i/expressions/face-icon-small-smile.gif" border="0">


<a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/DrugDevelopmentPipeline/">http://www.cff.org/research/DrugDevelopmentPipeline/</a>
 

NoExcuses

New member
Marla you have probably seen this before but the CFF updates this pipeline regularly <img src="i/expressions/face-icon-small-smile.gif" border="0">


<a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/DrugDevelopmentPipeline/">http://www.cff.org/research/DrugDevelopmentPipeline/</a>
 

NoExcuses

New member
Marla you have probably seen this before but the CFF updates this pipeline regularly <img src="i/expressions/face-icon-small-smile.gif" border="0">


<a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/DrugDevelopmentPipeline/">http://www.cff.org/research/DrugDevelopmentPipeline/</a>
 

NoExcuses

New member
Marla you have probably seen this before but the CFF updates this pipeline regularly <img src="i/expressions/face-icon-small-smile.gif" border="0">


<a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/DrugDevelopmentPipeline/">http://www.cff.org/research/DrugDevelopmentPipeline/</a>
 

NoExcuses

New member
Marla you have probably seen this before but the CFF updates this pipeline regularly <img src="i/expressions/face-icon-small-smile.gif" border="0">
<br />
<br />
<br /><a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/DrugDevelopmentPipeline/">http://www.cff.org/research/DrugDevelopmentPipeline/</a>
 

Faust

New member
My thoughts regarding PTC124: This will be wonderful news for the smaller percentage of CF's with mutations ending in X (from what I have been told, those are the only nonsense mutations). For the others without these mutations, it will mean nothing besides knowing others are technically being cured.
 

Faust

New member
My thoughts regarding PTC124: This will be wonderful news for the smaller percentage of CF's with mutations ending in X (from what I have been told, those are the only nonsense mutations). For the others without these mutations, it will mean nothing besides knowing others are technically being cured.
 

Faust

New member
My thoughts regarding PTC124: This will be wonderful news for the smaller percentage of CF's with mutations ending in X (from what I have been told, those are the only nonsense mutations). For the others without these mutations, it will mean nothing besides knowing others are technically being cured.
 

Faust

New member
My thoughts regarding PTC124: This will be wonderful news for the smaller percentage of CF's with mutations ending in X (from what I have been told, those are the only nonsense mutations). For the others without these mutations, it will mean nothing besides knowing others are technically being cured.
 

Faust

New member
My thoughts regarding PTC124: This will be wonderful news for the smaller percentage of CF's with mutations ending in X (from what I have been told, those are the only nonsense mutations). For the others without these mutations, it will mean nothing besides knowing others are technically being cured.
<br />
<br />
<br />
 
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