PTC124

anonymous

New member
My son was the first patient in the US to receive the drug and it definitely showed an improvement in his nasal pd but more so in the nasal scrapings they tested. We have been through with the study since December and they have to finish the study in all of the sites. At that time, from what Im told they will study the findings and submit it to the FDA and then if everything is good and it is approved it will go into the next phase with more people- I think they will also allow younger patients to be in the study. We go back to clinic in 3 weeks and I hope to talk to the dr who is in charge of the research then. Susan
 
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