JennyCoulon
New member
That is very promising and exciting.
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PTC124
- Thread starter HRod
- Start date
JennyCoulon
New member
That is very promising and exciting.
JennyCoulon
New member
That is very promising and exciting.
JennyCoulon
New member
That is very promising and exciting.
JennyCoulon
New member
That is very promising and exciting.
L
lhkraus
Guest
You should note, though, that PTC 124 will only "fix" CF genes that have a "nonsense mutation." That affects about 10% of CFers. As a general rule, mutations that end in X are nonsense mutations, but there are others. Check the PTC website for more info. Right now they are in the planning phase for a second round of phase 2 trials. After that, they'd have to do phase 3 trials before it can be marketed (Assuming it's successful). The results so far have been promising -- my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!
L
lhkraus
Guest
You should note, though, that PTC 124 will only "fix" CF genes that have a "nonsense mutation." That affects about 10% of CFers. As a general rule, mutations that end in X are nonsense mutations, but there are others. Check the PTC website for more info. Right now they are in the planning phase for a second round of phase 2 trials. After that, they'd have to do phase 3 trials before it can be marketed (Assuming it's successful). The results so far have been promising -- my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!
L
lhkraus
Guest
You should note, though, that PTC 124 will only "fix" CF genes that have a "nonsense mutation." That affects about 10% of CFers. As a general rule, mutations that end in X are nonsense mutations, but there are others. Check the PTC website for more info. Right now they are in the planning phase for a second round of phase 2 trials. After that, they'd have to do phase 3 trials before it can be marketed (Assuming it's successful). The results so far have been promising -- my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!
L
lhkraus
Guest
You should note, though, that PTC 124 will only "fix" CF genes that have a "nonsense mutation." That affects about 10% of CFers. As a general rule, mutations that end in X are nonsense mutations, but there are others. Check the PTC website for more info. Right now they are in the planning phase for a second round of phase 2 trials. After that, they'd have to do phase 3 trials before it can be marketed (Assuming it's successful). The results so far have been promising -- my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!
L
lhkraus
Guest
You should note, though, that PTC 124 will only "fix" CF genes that have a "nonsense mutation." That affects about 10% of CFers. As a general rule, mutations that end in X are nonsense mutations, but there are others. Check the PTC website for more info. Right now they are in the planning phase for a second round of phase 2 trials. After that, they'd have to do phase 3 trials before it can be marketed (Assuming it's successful). The results so far have been promising -- my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!
MargaritaChic
New member
<div class="FTQUOTE"><begin quote><i>Originally posted by: <b>lhkraus</b></i>
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote></div>
DITTO!
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote></div>
DITTO!
MargaritaChic
New member
<div class="FTQUOTE"><begin quote><i>Originally posted by: <b>lhkraus</b></i>
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote></div>
DITTO!
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote></div>
DITTO!
MargaritaChic
New member
<div class="FTQUOTE"><begin quote><i>Originally posted by: <b>lhkraus</b></i>
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote></div>
DITTO!
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote></div>
DITTO!
MargaritaChic
New member
<div class="FTQUOTE"><begin quote><i>Originally posted by: <b>lhkraus</b></i>
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote>
DITTO!
my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote>
DITTO!
MargaritaChic
New member
<div class="FTQUOTE"><begin quote><i>Originally posted by: <b>lhkraus</b></i>
<br />my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote>
<br />
<br />DITTO!
<br />
<br />
<br />my heart expands when I think my daughter may be "cured" of her symptoms with just a pill!</end quote>
<br />
<br />DITTO!
<br />
<br />