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Thanks! I will follow this study. But not sure - as we are in Switzerland we have limited access to the studies and we just there was just the chance to participate in the current 661 combo study for DD508 and residual function. But as my son being too young no way of getting into. Status is...

Oh, which other hetero arm do you mean? I would even consider to try to get him off-label on 809/orkambi as soon as he turns 12 next April....

If they included specific mutations they would have to mention it, right? I would suppose their inclusion parameters are clearly stated and they include every mutation accordingly. My son has R347P which is was not mentioned to respond in the in vitro studies. In real life, my son (11 years) is...

R347p Hi - may I ask are you still on Kalydeco and still keeping the good results? We are in the same boat with R347P - Class 4/Conductance, not responsive in vitro but also PS and very keen to try Kalydecco or - as DF508 as well - the combination drug.

Steve, my son has DeltaF508 and R347P (class IV). The only thing I know about class IV mutations is that patients are often pancreatic sufficient (and my son is). Do you have any insight about this specific mutation? Thank you.