I have recently started on Kalydeco. I have two rare genetic mutations and one is a residual function mutation. However, neither are on label because they are very rare. I have Q493* (there are 288 other people in the CFTR2 database with this mutation) and D513G (there are 7 other people in...
I have recently started on Kalydeco. I have two rare genetic mutations and one is a residual function mutation. However, neither are on label because they are very rare. I have Q493* (there are 288 other people in the CFTR2 database with this mutation) and D513G (there are 7 other people in...
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