Some promising news from European Cystic Fibrosis Society (ECFS) president and Cystic Fibrosis Trust professor Stuart Elborn:
Kalydeco (Ivacaftor) is the first drug treatment that not only treats the symptoms, but also the underlying causes of CF, and is currently approved for patients with the ‘celtic gene’ mutation carried by about four percent of all patients. The two phase 3 studies performed by Vertex tested the combination of ivacaftor and lumacaftor in over 1,100 patients worldwide, built on previous studies of ivacaftor in patients with G551D and other related mutations.
Read full source.
Kalydeco (Ivacaftor) is the first drug treatment that not only treats the symptoms, but also the underlying causes of CF, and is currently approved for patients with the ‘celtic gene’ mutation carried by about four percent of all patients. The two phase 3 studies performed by Vertex tested the combination of ivacaftor and lumacaftor in over 1,100 patients worldwide, built on previous studies of ivacaftor in patients with G551D and other related mutations.
Read full source.