Aboveallislove
Super Moderator
Orkambi is poised to be approved by the fda tomorrow or soon after but only for a label use of 12 and older for those with teo copies of df508. I came across this great info on what other mutations it could also help...and for some mutations even better than df508. This blog summarizes part and at the end it links to her earlier summary of other mutations. https://sixtyfiverosesblog.wordpress.com/2013/10/18/how-does-vx809-help-f508del-part-2/
If you have two mutations it can help and want to brain storm on how to proceed off label, let me know.
If you have two mutations it can help and want to brain storm on how to proceed off label, let me know.