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Cystic Fibrosis
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CFTR Modulation and Gene Therapy Talk
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A
V520f mutation
amykay1965
Sep 15, 2012
Replies
1
Views
2K
Sep 21, 2012
kyeev
K
A
V520f
amykay1965
Sep 15, 2012
Replies
3
Views
3K
Sep 21, 2012
kyeev
K
J
Can sweat chloride numbers drop on their own?
JENNYC
Sep 19, 2012
Replies
6
Views
2K
Sep 20, 2012
Aboveallislove
A
E
How to tell what trials or medicines may apply to mutations?
ethandley
Sep 19, 2012
Replies
0
Views
1K
Sep 19, 2012
ethandley
E
C
Ivacaftor and splicing mutations..
cftrsplicing
Sep 17, 2012
Replies
6
Views
4K
Sep 18, 2012
dramamama
D
J
Abby update
JENNYC
Jul 26, 2012
Replies
12
Views
4K
Sep 13, 2012
JENNYC
J
M
Pregnancy and Kalydeco
musclemania70
Sep 5, 2012
Replies
8
Views
3K
Sep 11, 2012
Allansarmy
A
M
Cys866Tyr or Cystic Fibrosis Variant?
MaggieRose
Sep 5, 2012
Replies
2
Views
2K
Sep 6, 2012
MaggieRose
M
K
D508/R117 mutations
kittenface
Jul 19, 2012
2
Replies
28
Views
11K
Sep 6, 2012
marcijo
M
A
Kalydeco and cataracts
albino15
Aug 29, 2012
Replies
1
Views
2K
Aug 29, 2012
JENNYC
J
A
For those on Kalydeco--help those in UK and Ireland
Aboveallislove
Aug 24, 2012
Replies
3
Views
2K
Aug 29, 2012
draz91
D
J
PTC 124 updates?
JENNYC
Aug 29, 2012
Replies
0
Views
1K
Aug 29, 2012
JENNYC
J
E
questions about therapies for g551ds, who are on Kalydeco
echolaura
Jul 25, 2012
Replies
10
Views
4K
Aug 20, 2012
cindylou
C
G
Kalydeco gets EMA approval (Europe) & Vertex has applied to the TGA (Australia) and the TPD (Canada)
GenH
Jul 27, 2012
Replies
4
Views
2K
Aug 19, 2012
CyrilCrodius
C
S
Double DF508
sierradavis
Aug 9, 2012
Replies
6
Views
5K
Aug 17, 2012
kitomd21
K
S
Starting Kalydeco Today
Sundown
Jun 30, 2012
Replies
14
Views
5K
Aug 12, 2012
Lena Bean
L
C
Kalydeco users help needed
chezza
Jul 20, 2012
Replies
2
Views
2K
Jul 23, 2012
JENNYC
J
N
DF508 question
Nikole
Apr 16, 2012
Replies
4
Views
2K
Jul 23, 2012
skydiverchic
S
S
Normal Liver Enzymes after 10 weeks on Kaly
saveferris2009
May 31, 2012
Replies
8
Views
3K
Jul 22, 2012
musclemania70
M
J
Abby Sweat Tests
JENNYC
Jul 19, 2012
Replies
10
Views
3K
Jul 22, 2012
LittleLab4CF
L
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