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To have a nonsense mutation, at least one of your two mutations has to end in X. For example, one could be DeltaF508 and the other might be G542X.

PTC Therapeutics Announces Interim Phase 2 Results of PTC124 in Cystic Fibrosis SOUTH PLAINFIELD, NJ - April 4, 2006 - PTC Therapeutics, Inc. (PTC), a biopharmaceutical company focused on the discovery, development, and commercialization of orally administered, proprietary small-molecule...

PTC Therapeutics Announces Interim Phase 2 Results of PTC124 in Cystic Fibrosis SOUTH PLAINFIELD, NJ - April 4, 2006 - PTC Therapeutics, Inc. (PTC), a biopharmaceutical company focused on the discovery, development, and commercialization of orally administered, proprietary small-molecule...

Has anyone heard any news on how the trials are going? Is this drug working? Thanks, Brian

<blockquote>Quote<br><hr>My son finished the trial on December 27th- he participated in Birmingham Alabama. It definitely showed promise. They are also getting good results in Israel. At our last appt there were two more people enrolled in Bham- may be more now. I dont think anymore of the US...

<blockquote>Quote<br><hr>My son finished the trial on December 27th- he participated in Birmingham Alabama. It definitely showed promise. They are also getting good results in Israel. At our last appt there were two more people enrolled in Bham- may be more now. I dont think anymore of the US...

While it is true that the drug would just fix one of the mutations, that is all that is needed to cure CF. If we just had one mutation then we would be a carrier and not have full blown CF.

While it is true that the drug would just fix one of the mutations, that is all that is needed to cure CF. If we just had one mutation then we would be a carrier and not have full blown CF.

Is anyone participating in the phase 2 trials of PTC124? Brian

Is anyone participating in the phase 2 trials of PTC124? Brian

Thanks Sean. I am a little confused with the nebulizing part. When you put the drops in your neb... what do you put in the neb with the drops? I saw the link to the facial inhaler you got at Target. I will order that. Now, I know you don't put tap water in it. How do you sterilize the...

I have been reading through all the postings on OOO. It sounds like it has great possibilities. A couple questions... 1) Has anyone been taking it since the original post? Are you having positive effects? 2) It looks like SeanDavis was originally taking it through his nebulizer but then...