Atalauren

[Rebjane]

http://ptct.client.shareholder.com/releasedetail.cfm?ReleaseID=681445

 

[Lastar1]

Thank you. Just saw this as well. I have only been waiting for 10 YEARS! Hope this is good enough for FDA approval.
Lisa, mom to 3, one 11 year old w/cf

 

[saveferris2009]

Lisa, from drug discovery to market, drugs usually take 10-15 years.

This is great news for these patients! Fingers crossed!

 

[Rebjane]

I wonder what the combo of Atalauren and Kalydeco would do together?

 

[musclemania70]

They must have been eager to compete with recent Vertex results.

 

[echolaura]

Does anybody know what the data given so far, translates to percentages? All I have heard is that there is "decrease in decline of function" and decreased exacerbations, but I get the feeling that the results haven't been as dramatic as the avg 10% seen with Kalydeco (ivacaftor) Congrats to all you nonsense mutations!

 

[saveferris2009]

the link that was posted by the OP has the %