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Ataluren (PTC124) Are study participants close to finishing?
- Thread starter Gnome
- Start date
Hello,
I, too, am interested in Ataluren/PTC 124 as my 1.5 year old boy has a nonsense mutation (R1162X). I checked out the PTC website and the clinical trials website; I learned that the Phase 3 Ataluren trial is still underway with an expected completion date of March 2012. I hope for the best.
[On a side note: I'm glad to see that we can openly discuss drugs in the pipeline on this forum. Right after my son was born, I posted an article about the encouraging signs of Vertex' trials/tests. One of the moderators sent me a message, accused me of being an employee of a drug company and I was banned from this website. I've created a new username as I really like this site and hope to contribute. Hopefully, I won't be banned again. I'll say in no uncertain terms: I have NO connection to any drug company. Thanks.]
I, too, am interested in Ataluren/PTC 124 as my 1.5 year old boy has a nonsense mutation (R1162X). I checked out the PTC website and the clinical trials website; I learned that the Phase 3 Ataluren trial is still underway with an expected completion date of March 2012. I hope for the best.
[On a side note: I'm glad to see that we can openly discuss drugs in the pipeline on this forum. Right after my son was born, I posted an article about the encouraging signs of Vertex' trials/tests. One of the moderators sent me a message, accused me of being an employee of a drug company and I was banned from this website. I've created a new username as I really like this site and hope to contribute. Hopefully, I won't be banned again. I'll say in no uncertain terms: I have NO connection to any drug company. Thanks.]
Hello,
I, too, am interested in Ataluren/PTC 124 as my 1.5 year old boy has a nonsense mutation (R1162X). I checked out the PTC website and the clinical trials website; I learned that the Phase 3 Ataluren trial is still underway with an expected completion date of March 2012. I hope for the best.
[On a side note: I'm glad to see that we can openly discuss drugs in the pipeline on this forum. Right after my son was born, I posted an article about the encouraging signs of Vertex' trials/tests. One of the moderators sent me a message, accused me of being an employee of a drug company and I was banned from this website. I've created a new username as I really like this site and hope to contribute. Hopefully, I won't be banned again. I'll say in no uncertain terms: I have NO connection to any drug company. Thanks.]
I, too, am interested in Ataluren/PTC 124 as my 1.5 year old boy has a nonsense mutation (R1162X). I checked out the PTC website and the clinical trials website; I learned that the Phase 3 Ataluren trial is still underway with an expected completion date of March 2012. I hope for the best.
[On a side note: I'm glad to see that we can openly discuss drugs in the pipeline on this forum. Right after my son was born, I posted an article about the encouraging signs of Vertex' trials/tests. One of the moderators sent me a message, accused me of being an employee of a drug company and I was banned from this website. I've created a new username as I really like this site and hope to contribute. Hopefully, I won't be banned again. I'll say in no uncertain terms: I have NO connection to any drug company. Thanks.]
Hello,
<br />
<br />I, too, am interested in Ataluren/PTC 124 as my 1.5 year old boy has a nonsense mutation (R1162X). I checked out the PTC website and the clinical trials website; I learned that the Phase 3 Ataluren trial is still underway with an expected completion date of March 2012. I hope for the best.
<br />
<br />[On a side note: I'm glad to see that we can openly discuss drugs in the pipeline on this forum. Right after my son was born, I posted an article about the encouraging signs of Vertex' trials/tests. One of the moderators sent me a message, accused me of being an employee of a drug company and I was banned from this website. I've created a new username as I really like this site and hope to contribute. Hopefully, I won't be banned again. I'll say in no uncertain terms: I have NO connection to any drug company. Thanks.]
<br />
<br />I, too, am interested in Ataluren/PTC 124 as my 1.5 year old boy has a nonsense mutation (R1162X). I checked out the PTC website and the clinical trials website; I learned that the Phase 3 Ataluren trial is still underway with an expected completion date of March 2012. I hope for the best.
<br />
<br />[On a side note: I'm glad to see that we can openly discuss drugs in the pipeline on this forum. Right after my son was born, I posted an article about the encouraging signs of Vertex' trials/tests. One of the moderators sent me a message, accused me of being an employee of a drug company and I was banned from this website. I've created a new username as I really like this site and hope to contribute. Hopefully, I won't be banned again. I'll say in no uncertain terms: I have NO connection to any drug company. Thanks.]
L
lhkraus
Guest
I'd also recommend going to the PTC website for information. If you email them a question, they do respond promptly, which is nice (and I also am a parent of a child with a nonsense mutation, not a drug company rep!)
L
lhkraus
Guest
I'd also recommend going to the PTC website for information. If you email them a question, they do respond promptly, which is nice (and I also am a parent of a child with a nonsense mutation, not a drug company rep!)
L
lhkraus
Guest
I'd also recommend going to the PTC website for information. If you email them a question, they do respond promptly, which is nice (and I also am a parent of a child with a nonsense mutation, not a drug company rep!)
I hope it wasn't this site you were originally banned from. I've been here for years and there's always been open discussion of drugs in the pipeline. Suggestions and experiences of different (alternative) treatments as well.
Both my girls have double nonsense mutations. PTC will add you to their e-mailings to keep up to date with how Ataluren is doing in their various clinical trials. I will add, you will get info on the other diseases it is in trial for as well because it is not specific for just CF.
Both my girls have double nonsense mutations. PTC will add you to their e-mailings to keep up to date with how Ataluren is doing in their various clinical trials. I will add, you will get info on the other diseases it is in trial for as well because it is not specific for just CF.
I hope it wasn't this site you were originally banned from. I've been here for years and there's always been open discussion of drugs in the pipeline. Suggestions and experiences of different (alternative) treatments as well.
Both my girls have double nonsense mutations. PTC will add you to their e-mailings to keep up to date with how Ataluren is doing in their various clinical trials. I will add, you will get info on the other diseases it is in trial for as well because it is not specific for just CF.
Both my girls have double nonsense mutations. PTC will add you to their e-mailings to keep up to date with how Ataluren is doing in their various clinical trials. I will add, you will get info on the other diseases it is in trial for as well because it is not specific for just CF.
I hope it wasn't this site you were originally banned from. I've been here for years and there's always been open discussion of drugs in the pipeline. Suggestions and experiences of different (alternative) treatments as well.
<br />
<br />Both my girls have double nonsense mutations. PTC will add you to their e-mailings to keep up to date with how Ataluren is doing in their various clinical trials. I will add, you will get info on the other diseases it is in trial for as well because it is not specific for just CF.
<br />
<br />Both my girls have double nonsense mutations. PTC will add you to their e-mailings to keep up to date with how Ataluren is doing in their various clinical trials. I will add, you will get info on the other diseases it is in trial for as well because it is not specific for just CF.
M
Mommafirst
Guest
I've been trying to keep up with the Atalauren stuff too, I've heard that the results were more promising in studies abroad than here (in the US) -- but that they weren't sure why there would be a difference. I hope it was just a study error in the US and that this is still a promising drug. My daughter also has a nonsense mutation.
M
Mommafirst
Guest
I've been trying to keep up with the Atalauren stuff too, I've heard that the results were more promising in studies abroad than here (in the US) -- but that they weren't sure why there would be a difference. I hope it was just a study error in the US and that this is still a promising drug. My daughter also has a nonsense mutation.