Hi all,
Maybe I missed something here, but last I had heard the drug PTC 124 was really promising for those with mutations that are nonsense (I think that means they end in a X.) I was looking on the drug pipeline of the foundations website and I didn't see it mentioned at all! Is it renamed or no longer being researched? I was really hopeful for that drug!
Thanks,
Zoe mom to Kate wCF
Maybe I missed something here, but last I had heard the drug PTC 124 was really promising for those with mutations that are nonsense (I think that means they end in a X.) I was looking on the drug pipeline of the foundations website and I didn't see it mentioned at all! Is it renamed or no longer being researched? I was really hopeful for that drug!
Thanks,
Zoe mom to Kate wCF