R117h kalydeco FDA committee meeting

[Aboveallislove]

Not sure if any with r117h on here have used kalydeco but the upcoming fda committee meeting is looking at expanding label. They take written submissions so if you or a loved one has used and benefitted it might be worthwhile to send a personal testimonial. Here's the link http://www.fda.gov/AdvisoryCommittees/Calendar/ucm417332.htm

 

[stephen]

Aboveallislove,

Thanks for the heads up.

Although I don't have the R117H mutation, I did send an email to to the FDA Advisory Committee at PADAC@fda.hhs.gov outlining my experiences with Kalydeco and asking them to consider investigating its approval for additional CF mutations.

 

[ladybird]

Are they looking at it for R117C?