vertex submitted its application today for double f508del to the FDA and EU

[ClassyMike]

http://www.cff.org/aboutCFFoundatio...rtex-Submits-Combination-Drug-Application.cfm

This is the first time i've been excited in a long time! i know it's still a ways to go, but very cool.

 

[triples15]

I saw that today too! So amazing!

It seems like the FDA is has been good to Vertex and vice verse, so I'm hoping it goes quickly and smoothly.

I don't have double delta, but I'm so excited for those that do! It's just an exciting time in general, and I'm hoping it won't be terribly long before there's something available for all of us!!

Thanks for posting!

Autumn 34 w/CF

 

[Oboe]

In recognition of the immediate needs of some people with CF, Vertex is working to make the combination of lumacaftor and ivacaftor available to people ages 12 and older who have two copies of the F508del mutation, are in critical medical need and meet additional eligibility criteria in the first quarter of 2015.

Hopefully, as someone with roughly 22% FEV1, I qualify for that. I assume the red tape'll be a pain or it won't be available in my region or something, though.

 

[joannemk]

My daughter might have been helped by it but she died in July.Too late for her.

 

[Aboveallislove]

Oh, mom. I am so sorry for your loss.

 

[Gammaw]

Bless you Joanne. We all pray for cures before it's too late. Breathe easy.