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How optimistic are you about the new drugs in the pipeline?
- Thread starter dlo2977
- Start date
Just to second ymikhale, while I have heard great things on VX770 the reality is that we are very early in the process. I would love to see some of these drugs make it to production; however, drug companies get $$ by selling their products, not being realistic.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote></div>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote></div>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Just to second ymikhale, while I have heard great things on VX770 the reality is that we are very early in the process. I would love to see some of these drugs make it to production; however, drug companies get $$ by selling their products, not being realistic.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote></div>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote></div>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Just to second ymikhale, while I have heard great things on VX770 the reality is that we are very early in the process. I would love to see some of these drugs make it to production; however, drug companies get $$ by selling their products, not being realistic.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote></div>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote></div>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Just to second ymikhale, while I have heard great things on VX770 the reality is that we are very early in the process. I would love to see some of these drugs make it to production; however, drug companies get $$ by selling their products, not being realistic.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Per CFF information the Phase 2 results for VX770 were:
<div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote>
With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
Just to second ymikhale, while I have heard great things on VX770 the reality is that we are very early in the process. I would love to see some of these drugs make it to production; however, drug companies get $$ by selling their products, not being realistic.
<br />
<br />Per CFF information the Phase 2 results for VX770 were:
<br />
<br /><div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote>
<br />
<br />With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
<br />
<br />Per CFF information the Phase 2 results for VX770 were:
<br />
<br /><div class="FTQUOTE"><begin quote>This was a small, short-term study with 39 cystic fibrosis patients over a 14-day or 28-day period. Additional trials are needed, but the early results are encouraging.</end quote>
<br />
<br />With 70,000 people worldwide estimated to have CF (per Vertex) & ~2800 w/G551D; there is a lot of work to be done to show that the Phase 2 results can be reproduced.
TestifyToLove
New member
Like a lung transplant or any other organ transplant, a liver transplant does not give a normal life expectancy. And, in our case, a liver transplant can only happen if he can also get a small bowel due to his meconium illeus, his small intestines is too short to hook in a new liver without a new small bowel as well.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
TestifyToLove
New member
Like a lung transplant or any other organ transplant, a liver transplant does not give a normal life expectancy. And, in our case, a liver transplant can only happen if he can also get a small bowel due to his meconium illeus, his small intestines is too short to hook in a new liver without a new small bowel as well.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
TestifyToLove
New member
Like a lung transplant or any other organ transplant, a liver transplant does not give a normal life expectancy. And, in our case, a liver transplant can only happen if he can also get a small bowel due to his meconium illeus, his small intestines is too short to hook in a new liver without a new small bowel as well.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
TestifyToLove
New member
Like a lung transplant or any other organ transplant, a liver transplant does not give a normal life expectancy. And, in our case, a liver transplant can only happen if he can also get a small bowel due to his meconium illeus, his small intestines is too short to hook in a new liver without a new small bowel as well.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
TestifyToLove
New member
Like a lung transplant or any other organ transplant, a liver transplant does not give a normal life expectancy. And, in our case, a liver transplant can only happen if he can also get a small bowel due to his meconium illeus, his small intestines is too short to hook in a new liver without a new small bowel as well.
<br />
<br />So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
<br />
<br />In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
<br />
<br />So, as I said, no I have very little hope that these new drugs will do much for *my* child's life. But also again, the bulk of his challenges are from what CF has done to his liver and not his lungs. Ironic actually. We focus so heavily on the lung issues, and certainly we are totally aggressive with his lungs here. But, for him, its the liver that will likely determine his life expectancy as well as quality of life.
<br />
<br />In the end, its all CF though. CF claimed a massive portion of his bowels before he was even born and claimed his liver before he was 3 months old. The rest of his life is about managing the aftermath of this disease. And I don't see any drug in the pipeline that would prevent what happened to him, which started before he was even born and anyone knew he had CF.
jbrandonAW
New member
I'm blindly optimistic...yeah I might be let down...but the hope has be so fired up about my health that I could explode. So Im going to continue to be optimistic that it will be out within 2-3 years...and that I could be really healthy in 5...
stupid to some but it keeps me alive ya know
stupid to some but it keeps me alive ya know
jbrandonAW
New member
I'm blindly optimistic...yeah I might be let down...but the hope has be so fired up about my health that I could explode. So Im going to continue to be optimistic that it will be out within 2-3 years...and that I could be really healthy in 5...
stupid to some but it keeps me alive ya know
stupid to some but it keeps me alive ya know
jbrandonAW
New member
I'm blindly optimistic...yeah I might be let down...but the hope has be so fired up about my health that I could explode. So Im going to continue to be optimistic that it will be out within 2-3 years...and that I could be really healthy in 5...
stupid to some but it keeps me alive ya know
stupid to some but it keeps me alive ya know
jbrandonAW
New member
I'm blindly optimistic...yeah I might be let down...but the hope has be so fired up about my health that I could explode. So Im going to continue to be optimistic that it will be out within 2-3 years...and that I could be really healthy in 5...
stupid to some but it keeps me alive ya know
stupid to some but it keeps me alive ya know
jbrandonAW
New member
I'm blindly optimistic...yeah I might be let down...but the hope has be so fired up about my health that I could explode. So Im going to continue to be optimistic that it will be out within 2-3 years...and that I could be really healthy in 5...
<br />
<br />stupid to some but it keeps me alive ya know
<br />
<br />stupid to some but it keeps me alive ya know