PTC Moving to phase III

S

saveferris2009

New member
Thanks to all who participated in Phase II studies of PTC 124 (ataluren), the drug is now moving to Phase III.

With so many drugs in the pipeline, this just further emphasizes the need for <b> <u>EVERYONE </u> to participate in CF clinical trials. </b> The more people participate, the faster these drugs can come to the market (all other things equal).

If you want to see which trials are in your area, go to the CFF website: <a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/ClinicalResearch/Find/
">http://www.cff.org/research/ClinicalResearch/Find/
</a>

From the CFF:

"Our biotech collaborator PTC Pharmaceuticals just announced their potential CF drug ataluren, which has shown promising results in earlier clinical trials, has moved into Phase 3 testing.

"CF patients who took ataluren (formerly PTC 124) in Phase 2 clinical trials showed improved lung function and decreased cough. The results suggest the drug improves the function of the faulty CFTR protein in people with CF - the underlying cause of the disease. Phase 3 trials will further evaluate the effectiveness and long-term safety of this potential therapy."
 
S

saveferris2009

New member
Thanks to all who participated in Phase II studies of PTC 124 (ataluren), the drug is now moving to Phase III.

With so many drugs in the pipeline, this just further emphasizes the need for <b> <u>EVERYONE </u> to participate in CF clinical trials. </b> The more people participate, the faster these drugs can come to the market (all other things equal).

If you want to see which trials are in your area, go to the CFF website: <a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/ClinicalResearch/Find/
">http://www.cff.org/research/ClinicalResearch/Find/
</a>

From the CFF:

"Our biotech collaborator PTC Pharmaceuticals just announced their potential CF drug ataluren, which has shown promising results in earlier clinical trials, has moved into Phase 3 testing.

"CF patients who took ataluren (formerly PTC 124) in Phase 2 clinical trials showed improved lung function and decreased cough. The results suggest the drug improves the function of the faulty CFTR protein in people with CF - the underlying cause of the disease. Phase 3 trials will further evaluate the effectiveness and long-term safety of this potential therapy."
 
S

saveferris2009

New member
Thanks to all who participated in Phase II studies of PTC 124 (ataluren), the drug is now moving to Phase III.

With so many drugs in the pipeline, this just further emphasizes the need for <b> <u>EVERYONE </u> to participate in CF clinical trials. </b> The more people participate, the faster these drugs can come to the market (all other things equal).

If you want to see which trials are in your area, go to the CFF website: <a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/ClinicalResearch/Find/
">http://www.cff.org/research/ClinicalResearch/Find/
</a>

From the CFF:

"Our biotech collaborator PTC Pharmaceuticals just announced their potential CF drug ataluren, which has shown promising results in earlier clinical trials, has moved into Phase 3 testing.

"CF patients who took ataluren (formerly PTC 124) in Phase 2 clinical trials showed improved lung function and decreased cough. The results suggest the drug improves the function of the faulty CFTR protein in people with CF - the underlying cause of the disease. Phase 3 trials will further evaluate the effectiveness and long-term safety of this potential therapy."
 
S

saveferris2009

New member
Thanks to all who participated in Phase II studies of PTC 124 (ataluren), the drug is now moving to Phase III.

With so many drugs in the pipeline, this just further emphasizes the need for <b> <u>EVERYONE </u> to participate in CF clinical trials. </b> The more people participate, the faster these drugs can come to the market (all other things equal).

If you want to see which trials are in your area, go to the CFF website: <a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/ClinicalResearch/Find/
">http://www.cff.org/research/ClinicalResearch/Find/
</a>

From the CFF:

"Our biotech collaborator PTC Pharmaceuticals just announced their potential CF drug ataluren, which has shown promising results in earlier clinical trials, has moved into Phase 3 testing.

"CF patients who took ataluren (formerly PTC 124) in Phase 2 clinical trials showed improved lung function and decreased cough. The results suggest the drug improves the function of the faulty CFTR protein in people with CF - the underlying cause of the disease. Phase 3 trials will further evaluate the effectiveness and long-term safety of this potential therapy."
 
S

saveferris2009

New member
Thanks to all who participated in Phase II studies of PTC 124 (ataluren), the drug is now moving to Phase III.
<br />
<br />With so many drugs in the pipeline, this just further emphasizes the need for <b> <u>EVERYONE </u> to participate in CF clinical trials. </b> The more people participate, the faster these drugs can come to the market (all other things equal).
<br />
<br />If you want to see which trials are in your area, go to the CFF website: <a target=_blank class=ftalternatingbarlinklarge href="http://www.cff.org/research/ClinicalResearch/Find/
">http://www.cff.org/research/ClinicalResearch/Find/
</a><br />
<br />
<br />From the CFF:
<br />
<br />"Our biotech collaborator PTC Pharmaceuticals just announced their potential CF drug ataluren, which has shown promising results in earlier clinical trials, has moved into Phase 3 testing.
<br />
<br />"CF patients who took ataluren (formerly PTC 124) in Phase 2 clinical trials showed improved lung function and decreased cough. The results suggest the drug improves the function of the faulty CFTR protein in people with CF - the underlying cause of the disease. Phase 3 trials will further evaluate the effectiveness and long-term safety of this potential therapy."
 
R

Rebjane

Super Moderator
I called the contact person listed yesterday about this trial. My daughter has one nonsense mutation. The closest trial is 5 hours away for us; not due to open up for about 2-3 months but we are seriously thinking about getting involved in this trial. Reading through the criteria listed my daughter meets the requirements except her PFT's are slightly higher that what they have listed; I guess you are to be between 40-90%. Her last PFT was 104%. Not sure if this woulod exclude her for the trial.
 
R

Rebjane

Super Moderator
I called the contact person listed yesterday about this trial. My daughter has one nonsense mutation. The closest trial is 5 hours away for us; not due to open up for about 2-3 months but we are seriously thinking about getting involved in this trial. Reading through the criteria listed my daughter meets the requirements except her PFT's are slightly higher that what they have listed; I guess you are to be between 40-90%. Her last PFT was 104%. Not sure if this woulod exclude her for the trial.
 
R

Rebjane

Super Moderator
I called the contact person listed yesterday about this trial. My daughter has one nonsense mutation. The closest trial is 5 hours away for us; not due to open up for about 2-3 months but we are seriously thinking about getting involved in this trial. Reading through the criteria listed my daughter meets the requirements except her PFT's are slightly higher that what they have listed; I guess you are to be between 40-90%. Her last PFT was 104%. Not sure if this woulod exclude her for the trial.
 
R

Rebjane

Super Moderator
I called the contact person listed yesterday about this trial. My daughter has one nonsense mutation. The closest trial is 5 hours away for us; not due to open up for about 2-3 months but we are seriously thinking about getting involved in this trial. Reading through the criteria listed my daughter meets the requirements except her PFT's are slightly higher that what they have listed; I guess you are to be between 40-90%. Her last PFT was 104%. Not sure if this woulod exclude her for the trial.
 
R

Rebjane

Super Moderator
I called the contact person listed yesterday about this trial. My daughter has one nonsense mutation. The closest trial is 5 hours away for us; not due to open up for about 2-3 months but we are seriously thinking about getting involved in this trial. Reading through the criteria listed my daughter meets the requirements except her PFT's are slightly higher that what they have listed; I guess you are to be between 40-90%. Her last PFT was 104%. Not sure if this woulod exclude her for the trial.
 
S

saveferris2009

New member
Sounds interesting! Chance are they'll pay for your transportation and/or overnight stays if needed.

Keep us posted! <img src="i/expressions/face-icon-small-smile.gif" border="0">
 
S

saveferris2009

New member
Sounds interesting! Chance are they'll pay for your transportation and/or overnight stays if needed.

Keep us posted! <img src="i/expressions/face-icon-small-smile.gif" border="0">
 
S

saveferris2009

New member
Sounds interesting! Chance are they'll pay for your transportation and/or overnight stays if needed.

Keep us posted! <img src="i/expressions/face-icon-small-smile.gif" border="0">
 
S

saveferris2009

New member
Sounds interesting! Chance are they'll pay for your transportation and/or overnight stays if needed.

Keep us posted! <img src="i/expressions/face-icon-small-smile.gif" border="0">
 
S

saveferris2009

New member
Sounds interesting! Chance are they'll pay for your transportation and/or overnight stays if needed.
<br />
<br />Keep us posted! <img src="i/expressions/face-icon-small-smile.gif" border="0">
 
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